Tek-102 Gene Therapy for Rett Syndrome (2025 Updates)
Tek-102, also known as TSHA-102, is a one-time investigational gene therapy for Rett syndrome that delivers a functional MECP2 gene using an engineered AAV9 vector. It is currently in Phase…
Tek-102, also known as TSHA-102, is a one-time investigational gene therapy for Rett syndrome that delivers a functional MECP2 gene using an engineered AAV9 vector. It is currently in Phase…